How scientists made the discoveries behind a game-changing gene therapy for sickle cell disease and won a $3-million Breakthrough Prize

Sickle cell disease is the scourge a person’s red blood cells. The inherited blood disorder, which disproportionately affects people in sub-Saharan Africa and India, can cause unbearable pain “crises” and extreme exhaustion. And until recently, there was no curative treatment. Now approved gene therapies for sickle cell disease (including sickle cell anemia, the most extreme…

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